MLD Gene Therapy - Milano Update
Dr. Alessandra Biffi, TIGET, San Rafaelle Institute
An update on the Phase I/II Milano Gene Therapy clinical trial, including 5 year data and discussion of next steps.
47 min, ©July 2015
The Premier Family Resource for Metachromatic Leukodystrophy Information & Support
Supporting Compassion for families, Awareness, Research, and Education.