Featured Therapies:
Gene Therapy ... Now Recruiting late juveniles! Approved for pre-symptomatic late infantiles and early juveniles in the EU, with pre-approval access in the US.
Enzyme Therapy ... Phase IIb late infantiles (fully recruited)
If you are seeking to cure MLD or want to know about metachromatic leukodystrophy (MLD), you've come to the right place! We C.A.R.E.®, we welcome you, and we're glad that you found us!
2023 MLD FAMILY CONFERENCE™
Knoxville, TN USA
July 14th-15th
Click here for details!
Often your arrival here comes at a time of great personal trauma due to a recent diagnosis or encounter with MLD. We want you to know that you can count on us for support, information and to help you get connected with others who are also on the MLD journey.
* Compassion will take you to the MLD Family™ pages where you can connect with others.
* Research updates the latest in efforts to treat and cure MLD.
* Education leads to MLD-101 where you will find a comprehensive, yet very readable, layman's overview of MLD.
MLD Foundation is a non-profit 501(c)(3) organization and appreciates your generous support. Please check out our Fundraisers and MLD Stuff in the boxes below:
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Strategic Partnership with AllStripes MLD Registry - Please Participate! Newborn Screening – Policy Presentation Reference Book Recommendation Leukodystrohy Consensus Paper – Follow our Blog– March, 2014 - Learn about our openNHS initiative for Natural History Studies >>More here. January, 2014 - new MLD Awareness video >>More here.
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